Abstract
As introduced in the previous chapter, the term “gene therapy” refers to a vast series of applications, both in vivo and ex vivo, based on the utilization of nucleic acids for therapeutic purposes.
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2.1 Protein-Coding Genes
Further Reading
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Giacca, M. (2010). Therapeutic Nucleic Acids. In: Gene Therapy. Springer, Milano. https://doi.org/10.1007/978-88-470-1643-9_2
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DOI: https://doi.org/10.1007/978-88-470-1643-9_2
Publisher Name: Springer, Milano
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