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Eighteen-year follow-up of the first Italian MPSI patient treated with bone marrow transplantation

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References

  1. Neufeld EF, Muenzer J . The Mucopolysaccharidoses. In: Scriver CR, Beaudet AL, Sly WS, Valle D (eds). The Metabolic and Molecular Bases of Inherited Disease, 8th edn, vol. III. McGraw-Hill: New York, 2001, pp 3421–3452.

    Google Scholar 

  2. Hobbs JR, Hugh-Jones K, Barrett AJ, Byrom N, Chambers D, Henry K et al. Reversal of clinical features of Hurler's disease and biochemical improvement after treatment by bone-marrow transplantation. Lancet 1981; 2: 709–712.

    Article  CAS  Google Scholar 

  3. Peters C, Steward CG . Hematopoietic cell transplantation for inherited metabolic diseases: an overview of outcomes and practice guidelines. Bone Marrow Transplant 2003; 31: 229–239.

    Article  CAS  PubMed  Google Scholar 

  4. Wraith JE . The first 5 years of clinical experience with laronidase enzyme replacement therapy for mucopolysaccharidosis I. Expert Opin Pharmacother 2005; 6: 489–506.

    Article  CAS  PubMed  Google Scholar 

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Correspondence to M Scarpa.

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Messina, C., Rampazzo, A., Cesaro, S. et al. Eighteen-year follow-up of the first Italian MPSI patient treated with bone marrow transplantation. Bone Marrow Transplant 41, 905–906 (2008). https://doi.org/10.1038/sj.bmt.1705988

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