Transplants of fibroblasts secreting high levels of β-glucuronidase decrease lesions in the brains of mice with Sly syndrome, a lysososmal storage disease (771–774).
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Sly, W., Vogler, C. Gene therapy for lysosomal storage disease: A no-brainer?. Nat Med 3, 719–720 (1997). https://doi.org/10.1038/nm0797-719
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DOI: https://doi.org/10.1038/nm0797-719
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