Expanded CAG repeats in the crosshairs

From

View current issue Submit your manuscript

Antisense oligomers targeted to CAG repeats allow allele-specific knockdown of the gene that causes Huntington's disease.

This is a preview of subscription content, log in via an institution to check access.

Price excludes VAT (USA)
Tax calculation will be finalised during checkout.

Instant access to the full article PDF.

Orr, H.T. & Zoghbi, H.Y. Annu. Rev. Neurosci. 30, 575–621 (2007).
Article CAS Google Scholar
Hu, J. et al. Nat. Biotechnol. 27, 478–484 (2009).
Article CAS Google Scholar
Snell, R.G. et al. Nat. Genet. 4, 393–397 (1993).
Article CAS Google Scholar
Miller, V.M. et al. Proc. Natl. Acad. Sci. USA 100, 7195–7200 (2003).
Article CAS Google Scholar
Schwarz, D.S. et al. PLoS Genet. 2, e140 (2006)
Article Google Scholar
van Bilsen, P.H. et al. Hum. Gene Ther. 19, 710–719 (2008).
Article CAS Google Scholar
Zhang, Y. et al. J. Neurochem. 108, 82–90 (2009).
Article CAS Google Scholar
Pfister, E.L. et al. Curr. Biol. published online, doi: 10.1016/j.cub.2009.003.030 (9 April 2009).
Alves, S. et al. PLoS ONE 3, e3341 (2008).
Article Google Scholar

Neil Aronin is at the University of Massachusetts Medical School, Worcester, Massachusetts, USA. Neil.Aronin@umassmed.edu,
Neil Aronin

Authors

Neil Aronin
View author publications
You can also search for this author in PubMed Google Scholar

Aronin, N. Expanded CAG repeats in the crosshairs. Nat Biotechnol 27, 451–452 (2009). https://doi.org/10.1038/nbt0509-451

Price excludes VAT (USA)
Tax calculation will be finalised during checkout.

Instant access to the full article PDF.