Orphan diseases: state of the drug discovery art Claude-Henry VolmarClaes WahlestedtShaun P. Brothers main topic 27 January 2016 Pages: 197 - 204
Pharmacological therapies for Angelman syndrome Wen-Hann TanLynne M. Bird main topic 12 January 2016 Pages: 205 - 218
Therapeutic strategies in adrenoleukodystrophy Bela R. TurkAnn B. MoserAli Fatemi main topic 10 May 2017 Pages: 219 - 226
Relapsing polychondritis: a chameleon among orphan diseases Sabine SchumacherHerwig Pieringer main topic 31 March 2017 Pages: 227 - 233
Metabolische Chirurgie oder konservative Maßnahmen zur Behandlung adipöser Typ 2-Diabetiker? Udo JahnThomas SchubertHeinz Jürgen Deuber übersicht 05 December 2016 Pages: 234 - 244