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Successful Haploidentical Stem Cell Transplantation with Post-Transplant Cyclophosphamide in a Severe Combined Immune Deficiency Patient: a First Report

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Acknowledgments

The authors would like to thank the patient’s family for their trust and collaboration.

Authorship Contributions

All authors have contributed to the manuscript in significant ways. M.O designed the research, interpreted data, and wrote the manuscript. F.M, M.BK, and H.K collaborated in the research design and clinical management of the patient. C.P performed molecular analysis. M.B designed the research, reviewed, and approved the manuscript.

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Authors and Affiliations

  1. Faculty of Medicine, University of Tunis El Manar, Tunis, Tunisia

    Monia Ouederni, Fethi Mellouli, Monia Ben Khaled & Mohamed Bejaoui

  2. Pediatric Immuno-Hematology Unit, Bone Marrow Transplantation Center, Tunis, Tunisia

    Monia Ouederni, Fethi Mellouli, Monia Ben Khaled & Mohamed Bejaoui

  3. Centre National de Greffe de Moelle Osseuse de Tunis, Bab Saadoun, 2 Rue Jbel lakhdar, 1002, Tunis, Tunisia

    Monia Ouederni

  4. National Center of Blood Transfusion, Tunis, Tunisia

    Houda Kaabi

  5. Study Center for Primary Immunodeficiencies, Necker-Enfants Malades Hospital, Assistance Publique Hôpitaux de Paris (APHP), Paris, France

    Capucine Picard

  6. Pediatric Immuno-Hematology Unit, Necker Children’s Hospital, APHP, Paris, France

    Capucine Picard

  7. INSERM UMR1163, Imagine Institute, University Paris Descartes, Necker Medical School, Sorbonne Paris Cité, Paris, France

    Capucine Picard

  8. Laboratory of the Human Genetics of Infectious Diseases, INSERM UMR1163, Imagine Institute, University Paris Descartes, Necker Medical School, Sorbonne Paris Cité, Paris, France

    Capucine Picard

Authors
  1. Monia Ouederni
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  2. Fethi Mellouli
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  3. Monia Ben Khaled
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  4. Houda Kaabi
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  5. Capucine Picard
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  6. Mohamed Bejaoui
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Corresponding author

Correspondence to Monia Ouederni.

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Conflict of Interest

The authors declare that they have no competing interests.

Human and Animal Rights

This article does not contain any studies involving animals performed by any of the authors.

Informed Consent

Informed consent was obtained from all individual participants included in the study.

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Ouederni, M., Mellouli, F., Khaled, M.B. et al. Successful Haploidentical Stem Cell Transplantation with Post-Transplant Cyclophosphamide in a Severe Combined Immune Deficiency Patient: a First Report. J Clin Immunol 36, 437–440 (2016). https://doi.org/10.1007/s10875-016-0293-2

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  • DOI: https://doi.org/10.1007/s10875-016-0293-2

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