Abstract
A nursery rhyme, which some of us learned when we were children brought tinker, tailor, soldier, and sailor together (Opie and Opie, 1951), rather like this volume, where its authors have been convened from many disciplines to describe how the diverse indexes of our individuality—our proteins—can be handled for biomedical purposes. My contribution to the mix is a chapter on strategies about enzyme replacement therapy; other authors provide the tactical details upon which the successful campaign for such treatment will depend.
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Scriver, C.R. (1977). A Biomedical View of Enzyme Replacement Strategies in Genetic Disease. In: Chang, T.M.S. (eds) Biomedical Applications of Immobilized Enzymes and Proteins. Springer, Boston, MA. https://doi.org/10.1007/978-1-4684-2610-6_10
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