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The Future of Gene Therapy

  • Conference paper
Human Gene Therapy: Current Opportunities and Future Trends

Part of the book series: Ernst Schering Research Foundation Workshop ((SCHERING FOUND,volume 43))

Abstract

Gene therapy can be defined as the introduction of genetic material into a particular cell or tissue type to alter the pattern of gene expression to produce a therapeutic effect. There are three critical components to consider in designing and optimizing a gene therapy strategy for the treatment of any disease: a vector to introduce the gene, a device and procedure for delivering the vector to the appropriate tissue or organ, and a therapeutic gene. Each component must be chosen or modified to best suit the specific characteristics of the particular disease of interest.

The comments and opinions in this paper reflect those of the author as an individual and do not necessarily represent the views of the U.S. National Institutes of Health, the Department of Health and Human Services, or the U.S. Government.

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  1. G. J. Nabel
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Editors and Affiliations

  1. Berlex Biosciences, 2600 Hilltop Drive, 94806, Richmond, CA, USA

    Gabor M. Rubanyi

  2. Department of Molecular Medicine, A.I. Virtanen Institute, University of Kuopio, P.O. Box 1627, 70211, Finland

    Seppo Ylä-Herttuala

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© 2003 Springer-Verlag Berlin Heidelberg

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Nabel, G.J. (2003). The Future of Gene Therapy. In: Rubanyi, G.M., Ylä-Herttuala, S. (eds) Human Gene Therapy: Current Opportunities and Future Trends. Ernst Schering Research Foundation Workshop, vol 43. Springer, Berlin, Heidelberg. https://doi.org/10.1007/978-3-662-05352-2_1

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  • DOI: https://doi.org/10.1007/978-3-662-05352-2_1

  • Publisher Name: Springer, Berlin, Heidelberg

  • Print ISBN: 978-3-662-05354-6

  • Online ISBN: 978-3-662-05352-2

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