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Bone marrow transplantation for immunodeficiency and genetic diseases

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Bone Marrow Transplantation

Part of the book series: Cancer Treatment and Research ((CTAR,volume 50))

Abstract

The use of allogeneic bone marrow transplantation to treat hematologic and oncologic diseases is well accepted [1,2]. Bone marrow transplantation is established therapy for genetic disorders involving the progeny of both lymphoid and hematopoietic stem cells (Table 1) [3]. The purpose of this chapter is to review the current status of allogeneic bone marrow transplantation for the treatment of genetic diseases, as well as to summarize the present status of gene therapy, a potential future therapy for genetic diseases.

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Authors
  1. Carl Lenarsky
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  2. Donald Kohn
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  3. Robertson Parkman
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Editors and Affiliations

  1. MD Anderson Cancer Center, Houston, Texas, USA

    Richard Champlin M.D.

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© 1990 Kluwer Academic Publishers

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Lenarsky, C., Kohn, D., Parkman, R. (1990). Bone marrow transplantation for immunodeficiency and genetic diseases. In: Champlin, R. (eds) Bone Marrow Transplantation. Cancer Treatment and Research, vol 50. Springer, Boston, MA. https://doi.org/10.1007/978-1-4613-1493-6_10

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  • DOI: https://doi.org/10.1007/978-1-4613-1493-6_10

  • Publisher Name: Springer, Boston, MA

  • Print ISBN: 978-1-4612-8803-9

  • Online ISBN: 978-1-4613-1493-6

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