Non-viral Gene Therapy pp 398-404 | Cite as
RNAi-Based Inhibition Specific for Mutant Alleles in Autosomal Dominant Diseases: Sequence-Dependent and -Independent Discrimination of Mutant and Wild-Type Alleles by siRNA
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Keywords
Amyotrophic Lateral Sclerosis Mutant Allele Autosomal Dominant Disease Familial Amyotrophic Lateral Sclerosis G93A SOD1
These keywords were added by machine and not by the authors. This process is experimental and the keywords may be updated as the learning algorithm improves.
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