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Diagnosing and monitoring treatment responses in patients with Niemann-Pick disease type C1 (NPC1) using fluorescence-based volumetric measurement of lysosomes. Science-Business eXchange 7, 206 (2014). https://doi.org/10.1038/scibx.2014.206
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DOI: https://doi.org/10.1038/scibx.2014.206