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Do we need marker gene studies in humans to improve clinical AAV gene therapy?

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Acknowledgements

I would like to thank Els Henckaerts, Michael Linden, Fadi Akar and Roger Hajjar for stimulating discussions. This work is supported by R01 HL131404 and a Trans-Atlantic Network of Excellence grant (14CVD03) from the Leducq Foundation.

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  1. Department of Medicine, Division of Cardiology, Cardiovascular Research Center and Graduate School of Biomedical Sciences, Icahn School of Medicine at Mount Sinai, New York, NY, USA

    T Weber

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Correspondence to T Weber.

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Weber, T. Do we need marker gene studies in humans to improve clinical AAV gene therapy?. Gene Ther 24, 72–73 (2017). https://doi.org/10.1038/gt.2016.84

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