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NICE. NICE draft guidance does not recommend risdiplam for treating spinal muscular atrophy. Internet Document : 3 Jun 2021. Available from: URL: https://www.nice.org.uk/news/article/nice-draft-guidance-does-not-recommend-risdiplam-for-treating-spinal-muscular-atrophy
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NICE draft guidance: risdiplam not recommended for spinal muscular atrophy. PharmacoEcon Outcomes News 880, 37 (2021). https://doi.org/10.1007/s40274-021-7795-8
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DOI: https://doi.org/10.1007/s40274-021-7795-8