Reference
NICE. NICE approves life-changing gene therapy for treating spinal muscular atrophy. Internet Document : 8 Mar 2021. Available from: URL: https://www.nice.org.uk/news/article/nice-approves-life-changing-gene-therapy-for-treating-spinal-muscular-atrophy
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NICE recommends Zolgensma for type 1 spinal muscular atrophy. PharmacoEcon Outcomes News 874, 35 (2021). https://doi.org/10.1007/s40274-021-7578-2
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DOI: https://doi.org/10.1007/s40274-021-7578-2