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Un-manipulated haploidentical transplant in Wiskott-Aldrich syndrome

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Abstract

Background

Allogeneic stem cell transplant is the only curative treatment for Wiskott-Aldrich syndrome.

Case characteristics

18-months-old boy with no sibling, cord blood or matched unrelated donor transplant options.

Outcome

Doing well 7 years after haploidentical stem cell transplantation using unmanipulated bone marrow as the stem cell source.

Message

Father as a haplo-identical donor is a feasible option.

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Author information

Authors and Affiliations

  1. Department of Clinical Haematology, Haemato-Oncology & Bone Marrow (Stem cell) Transplantation, Christian Medical College, Ludhiana, 141 008, Punjab, India

    M. Joseph John, Chepsy C. Philip & Amrith Mathew

  2. Department of Dermatology, Christian Medical College, Ludhiana, Punjab, India

    Abhilasha Williams

  3. Department of Haemato-Pathology, Christian Medical College, Ludhiana, Punjab, India

    Naveen Kakkar

Authors
  1. M. Joseph John
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  2. Chepsy C. Philip
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  3. Amrith Mathew
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  4. Abhilasha Williams
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  5. Naveen Kakkar
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Corresponding author

Correspondence to M. Joseph John.

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John, M.J., Philip, C.C., Mathew, A. et al. Un-manipulated haploidentical transplant in Wiskott-Aldrich syndrome. Indian Pediatr 54, 327–328 (2017). https://doi.org/10.1007/s13312-017-1097-z

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  • DOI: https://doi.org/10.1007/s13312-017-1097-z

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