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Rescuing Canavan disease: engineering the wrong cell at the right time

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Journal of Inherited Metabolic Disease

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References

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Correspondence to Morris H Baslow.

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This article does not contain any studies with human or animal subjects performed by the author.M.H. Baslow planned and wrote the article.

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M.H. Baslow has no conflict of interest.

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Communicated by: Ertan Mayatepek

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Baslow, M.H. Rescuing Canavan disease: engineering the wrong cell at the right time. J Inherit Metab Dis 40, 627–628 (2017). https://doi.org/10.1007/s10545-017-0038-2

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  • DOI: https://doi.org/10.1007/s10545-017-0038-2

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