Abstract
Assessment of joint health in hemophilia should be performed for clinical care and/or research purposes. It is advisable to collect data related to bleeding, structural or functional alterations, and changes in activities and participation, according to the International Classification of Functioning, Disability and Health (ICF). It is also useful to collect information on hematologic treatment consumption, health care utilization, and quality of life. In addition, outcome measurement tools based on the patient’s perspective are increasingly being developed. Multiple scales exist to quantify each of the above areas, generic or hemophilia-specific. The scales simply structure some of the most relevant information for a specific purpose. Therefore, they are a complement to the history, examination, and investigation of the patient and their symptoms, which should be carried out in a holistic manner. Currently, there is a very varied profile of people with hemophilia in terms of therapeutic opportunities and musculoskeletal condition. At the same time many options for outcome assessment have been described. This is why in practice hemophilia treatment centers must select the most appropriate instruments for their patients, instruments that should be unified in the future. In this chapter we will discuss the most commonly used assessment of joint health and outcome measures in hemophilia.
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De la Corte-Rodríguez, H., Liddle, A.D., Rodríguez-Merchán, E.C. (2022). Assessment of Joint Health and Outcome Measures in Hemophilia. In: Rodríguez-Merchán, E.C. (eds) Advances in Hemophilia Treatment . Springer, Cham. https://doi.org/10.1007/978-3-030-93990-8_11
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DOI: https://doi.org/10.1007/978-3-030-93990-8_11
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