2010

Muscle Gene Therapy

Editors:

ISBN: 978-1-4419-1205-3 (Print) 978-1-4419-1207-7 (Online)

Table of contents (16 chapters)

  1. Front Matter

    Pages i-xv

  2. No Access

    Book Chapter

    Pages 1-21

    Animal Models for Inherited Muscle Diseases

  3. No Access

    Book Chapter

    Pages 23-40

    In Utero Muscle Gene Transfer

  4. No Access

    Book Chapter

    Pages 41-53

    Gene Therapy for the Respiratory Muscles

  5. No Access

    Book Chapter

    Pages 55-68

    Muscular Dystrophy Gene Therapy in Small Animal Models

  6. No Access

    Book Chapter

    Pages 69-84

    Antisense-Mediated Exon Skipping for Duchenne Muscular Dystrophy

  7. No Access

    Book Chapter

    Pages 85-97

    Systemic Treatment of Duchenne Muscular Dystrophy by Antisense Oligomer-Induced Exon Skipping

  8. No Access

    Book Chapter

    Pages 99-115

    RNAi Therapy for Dominant Muscular Dystrophies and Other Myopathies

  9. No Access

    Book Chapter

    Pages 117-139

    Combinatorial Gene Therapy Strategies for Treating Muscular Dystrophies

  10. No Access

    Book Chapter

    Pages 141-162

    Duchenne Cardiomyopathy Gene Therapy

  11. No Access

    Book Chapter

    Pages 163-179

    Systemic Gene Delivery for Muscle Gene Therapy

  12. No Access

    Book Chapter

    Pages 181-204

    Modulating Immune Responses in Muscle Gene Therapy

  13. No Access

    Book Chapter

    Pages 205-218

    Delivering Large Therapeutic Genes for Muscle Gene Therapy

  14. No Access

    Book Chapter

    Pages 219-230

    Muscle as a Metabolic Factory for Gene Therapy

  15. No Access

    Book Chapter

    Pages 231-247

    Muscle as a Target for Genetic Vaccine

  16. No Access

    Book Chapter

    Pages 249-256

    Combining Stem Cells and Exon Skipping Strategy to Treat Muscular Dystrophy

  17. No Access

    Book Chapter

    Pages 257-267

    Gene Therapy Clinical Trials for Muscular Dystrophies

  18. Back Matter

    Pages 269-275